Decision-Making and Quality of Life Surrounding Hematologic Disease and Gene Therapy

Study Summary

Determine knowledge, attitudes, and beliefs among adult patients, and parents of pediatric patients, with transfusion dependent beta-thalassemia and sickle cell disease toward gene therapy to treat their or their child's illness, and to assess the likely impact of gene therapy on patients' quality of life.

Interventions

No interventions listed.

Study Locations

Facility	City	State	Country
Georgetown University Medical Center	Washington D.C.	District of Columbia	United States

Official Trial Information

View on ClinicalTrials.gov