Study Summary
The investigate will conduct a cohort study to compare the growth and development, metabolism, lifestyle behavior, and health-related quality of life among three groups: children with transfusion-dependent β-thalassemia (TDT) who have received gene therapy, TDT children with lifelong supportive therapy and healthy children.
Interested in this trial?
Submit an InquiryInterventions
Gene therapyGENETIC
Autologous edited hematopoietic stem cell transplantation
Study Locations
| Facility | City | State | Country |
|---|---|---|---|
| Regenerative Medicine Center | Tianjin | Tianjin Municipality | China |