NCT06292650

Prospective, Dose-Escalating, Investigator Initiated Trial to Evaluate the Safety and Efficacy of ZM-02 in Retinitis Pigmentosa

Study Summary

This is zM-02's safety, tOlerability, and efficacy in retinitis pigmentOsa first-in-humaN study (MOON). This trial is meant to evaluate the safety and efficacy of ZM-02 in Retinitis pigmentosa (RP) patients. Unilateral intravitreal injections (IVT) will be given into the subject's Study Eye.

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Interventions

ZM-02-LDRUG
rAAV-PsCatCh2.0 intravitreal injection of low dose
ZM-02-HDRUG
rAAV-PsCatCh2.0 intravitreal injection of high dose
ZM-02-SPROCEDURE
sham intravitreal injection of ZM-02 (not actual injection)

Study Locations

FacilityCityStateCountry
Beijing Tongren Hospital of Capital Medical UniversityBeijingBeijing MunicipalityChina

Official Trial Information

View on ClinicalTrials.gov

Data sourced from ClinicalTrials.gov. Last updated: April 14, 2026