Study Summary
This is an interventional study to evaluate safety and efficacy of AAV-hSMN1 in spinal muscular atrophy patients.
Interested in this trial?
Submit an InquiryInterventions
vesemnogene lantuparvovecBIOLOGICAL
Exploratory study evaluating the safety and efficacy of vesemnogene lantuparvovec in patients with SMA.
Study Locations
| Facility | City | State | Country |
|---|---|---|---|
| Kunming Hope of Health Hospital | Kunming | Yunnan | China |