A Multi-center Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of rAAV2-RPE65 Gene Therapy (LX101) in Subjects With Biallelic RPE65 Mutation-associated Inherited Retinal Dystrophy

Study Summary

The purpose of the study is to evaluate the safety, tolerability and efficacy of LX101 in subjects with biallelic RPE65 mutation-associated inherited retinal dystrophy.

Interventions

Study Locations

Facility	City	State	Country
Beijing Tongren Hospital, Capital Medical University	Beijing		China
Shanghai General Hospital	Shanghai		China

Official Trial Information

View on ClinicalTrials.gov