Phase I/IIa Intrathecal Gene Delivery Clinical Trial for IGHMBP2-Related Diseases

Study Summary

Open-label, single intrathecal injection study of a AAV9 vector carrying the IGHMBP2 gene for IGHMBP2-related diseases.

Interventions

Study Locations

Facility	City	State	Country
Nationwide Children's Hospital	Columbus	Ohio	United States

Official Trial Information

View on ClinicalTrials.gov