NCT05152732

Safety and Tolerability of VGB-R04 in Patients With Haemophilia B

Study Summary

An Open-Label, Non-Randomized, uncontrolled, single-dose pilot study of VGB-R04 in subjects with Hemophilia B.

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Interventions

VGB-R04GENETIC
A novel, bioengineered adeno-associated viral (AAV) vector carrying human factor IX variant

Study Locations

FacilityCityStateCountry
Blood diseases hospitalTianjinTianjin MunicipalityChina

Official Trial Information

View on ClinicalTrials.gov

Data sourced from ClinicalTrials.gov. Last updated: April 14, 2026