A Long-Term Follow-up Study to Evaluate the Safety, Tolerability, and Efficacy of Adeno-Associated Virus (AAV) rh10-Mediated Gene Transfer of Human Factor IX in Adults With Moderate/Severe to Severe Hemophilia B

Study Summary

A long-term follow-up study to evaluate the safety, tolerability, and efficacy of DTX101 in adult males with moderate/severe to severe hemophilia B.

Interventions

No interventions listed.

Study Locations

Facility	City	State	Country
Arkansas Children's Hospital	Little Rock	Arkansas	United States
UF CRC - Clinical Research Center	Gainesville	Florida	United States
University of Michigan Hospital and Health Systems	Ann Arbor	Michigan	United States
Haemophilia, Haemostasis & Thrombosis Centre	Basingstoke	Hampshire	United Kingdom
Manchester Haemophilia Comprehensive Care Center	Manchester		United Kingdom

Official Trial Information

View on ClinicalTrials.gov