NCT02556736

Phase I/IIa, Open-Label, Dose-Escalation Study of Safety and Tolerability of Intravitreal RST-001 in Patients With Advanced Retinitis Pigmentosa (RP)

Study Summary

All participants in phase 1 and phase 2a had hand motion visual acuity or worse. If efficacy was demonstrated from phase 1, better vision subjects could be enrolled; however, efficacy was not demonstrated.

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Interventions

AGN-151597DRUG
AGN-151597 is a gene therapeutic delivered by intravitreal injection

Study Locations

FacilityCityStateCountry
University of California San Francisco - Mission Bay /ID# 235717San FranciscoCaliforniaUnited States
Cincinnati Eye Institute- Edgewood /ID# 236713EdgewoodKentuckyUnited States
Duke Eye Center /ID# 235715DurhamNorth CarolinaUnited States
Retina Foundation of the Southwest /ID# 235199DallasTexasUnited States

Official Trial Information

View on ClinicalTrials.gov

Data sourced from ClinicalTrials.gov. Last updated: April 14, 2026