A Phase 1b, Multicenter, Single Dose Gene Transfer Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Girdle Muscular Dystrophy Type 2D/R3 Subjects in the United States

Study Summary

The primary objective of this study is to evaluate the safety of SRP-9004.

Interventions

Study Locations

Facility	City	State	Country
Nationwide Children's Hospital	Columbus	Ohio	United States
Children's Hospital of the King's Daughters	Norfolk	Virginia	United States

Official Trial Information

View on ClinicalTrials.gov