Study Summary
The purpose of the study is to assess the safety, tolerability, and efficacy of BBM-D101 to treat patients with Duchenne Muscular Dystrophy.
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BBM-D101GENETIC
BBM-D101 is a recombinant adeno-associated virus vector-based gene therapy for DMD treatment. It is a suspension for single intravenous (IV) infusion.
Study Locations
| Facility | City | State | Country |
|---|---|---|---|
| Shanghai Children's Medical Center Affiliated to Shanghai Jiao Tong University School of Medicine | Shanghai | Shanghai Municipality | China |