NCT06328764

A Clinical Study Evaluating the Safety and Efficacy of Autologous Peripheral Blood Hematopoietic Stem and Progenitor Cells (CS-101) Modified by Ex Vivo Base Editing to Induce γ-Globin Production in Treating Patients With β-Thalassemia

Study Summary

The goal of this open label, single-arm clinical study is to learn about the safety and efficacy of CS-101 in treating β-thalassemia.

Interested in this trial?

Submit an Inquiry

Interventions

CS-101GENETIC
Autologous CD34+ hematopoietic stem cell suspension modified by in vitro base editing technique

Study Locations

FacilityCityStateCountry
The First Affiliated Hospital of Guangxi Medical UniversityNanningGuangxiChina

Official Trial Information

View on ClinicalTrials.gov

Data sourced from ClinicalTrials.gov. Last updated: July 14, 2026