NCT06114056

A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD)

Study Summary

This study is a single-center, single-arm, non-randomized, open-label, non-controlled, dose-escalation, prospective clinical trial designed to assess the safety, tolerability, and preliminary efficacy of JWK007 injection in pediatric patients with Duchenne Muscular Dystrophy (DMD).

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Interventions

JWK007 Single intravenous infusion administrationBIOLOGICAL
Each patient receives a single intravenous infusion of JWK007 at a dose of 1.0 × 10\^14 vg/kg.

Study Locations

FacilityCityStateCountry
West China Hospital, Sichuan UniversityChengduSichuanChina

Official Trial Information

View on ClinicalTrials.gov

Data sourced from ClinicalTrials.gov. Last updated: April 14, 2026