Study Summary
The purpose of this study is to assess the risk of bleeding due to failure of expected pharmacological action of CSL222 in adults with severe or moderately severe hemophilia B with detectable pretreatment AAV5 Nabs.
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CSL222 (AAV5-hFIXco-Padua)GENETIC
Administered as a single IV infusion.
Study Locations
| Facility | City | State | Country |
|---|---|---|---|
| University of California, San Diego (UCSD) | San Diego | California | United States |
| University of Michigan | Ann Arbor | Michigan | United States |
| Royal Prince Alfred Hospital | Camperdown | New South Wales | Australia |
| Royal Brisbane Hospital | Herston | Queensland | Australia |
| Royal Adelaide Hospital | Adelaide | South Australia | Australia |
| The Alfred Hospital | Melbourne | Victoria | Australia |
| McMaster University - Hamilton | Hamilton | Ontario | Canada |
| Queen Mary Hospital | Hong Kong | Hong Kong | |
| Prince of Wales Hospital Chinese University of Hong Kong | Shatin | Hong Kong | |
| Sheba Medical Center | Tel Litwinsky | Israel | |
| Centro de Investigacion Clinica GRAMEL S.C. | Mexico City | Mexico City | Mexico |
| King Faisal Specialist Hospital and Research Center | Riyadh | Saudi Arabia | |
| National University Hospital | Singapore | Singapore | |
| Singapore General Hospital | Singapore | Singapore | |
| Haemophilia Comprehensive Care Centre | Johannesburg | South Africa | |
| Kyungpook National University Hospital | Daegu | South Korea | |
| Kyung Hee University Hospital at Gangdong | Seoul | South Korea | |
| Severance Hospital, Yonsei University Health System | Seoul | South Korea | |
| Tri-Service General Hospital | Taipei | Neihu District | Taiwan |
| Kaohsiung Medical University Chung-Ho Memorial Hospital (KMUH) | Kaohsiung City | Sanmin District | Taiwan |
| Changhua Christian Hospital (CCH) | Chang-hua | Taiwan | |
| Taichung Veterans General Hospital - | Taichung | Taiwan | |
| National Taiwan University Hospital | Taipei | Taiwan | |
| Ege University Medical Faculty | Bornova | Turkey (Türkiye) | |
| Gaziantep University Sahinbey Research and Practice Hospital | Gaziantep | Turkey (Türkiye) | |
| Özel Acibadem Adana Hastanesi | Seyhan | Turkey (Türkiye) |