Study Summary
The study is a single patient study intended to understand the effects of a gene-editing therapeutic to treat a rare mutation of Duchenne muscular dystrophy.
Interested in this trial?
Submit an InquiryInterventions
CRD-TMH-001DRUG
Participant will receive a single dose of CRD-TMH-001 administered via intravenous injection.
Study Locations
| Facility | City | State | Country |
|---|---|---|---|
| UMass Chan Medical School | Worcester | Massachusetts | United States |