Study Summary
The study is a single patient study intended to understand the effects of a gene-editing therapeutic to treat a rare mutation of Duchenne muscular dystrophy.
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CRD-TMH-001DRUG
Participant will receive a single dose of CRD-TMH-001 administered via intravenous injection.
Study Locations
| Facility | City | State | Country |
|---|---|---|---|
| UMass Chan Medical School | Worcester | Massachusetts | United States |