NCT04626674

An Open-Label, Systemic Gene Delivery Study Using Commercial Process Material to Evaluate the Safety of and Expression From SRP-9001 in Subjects With Duchenne Muscular Dystrophy (ENDEAVOR)

Study Summary

This is an open-label gene transfer therapy study evaluating the safety of and expression from delandistrogene moxeparvovec in participants with DMD. The maximum participant duration for this study is 156 weeks.

Want to learn more about this trial?

Request More Info

Interventions

delandistrogene moxeparvovecGENETIC
Single IV infusion of delandistrogene moxeparvovec

Study Locations

FacilityCityStateCountry
Arkansas Children's HospitalLittle RockArkansasUnited States
Stanford UniversityPalo AltoCaliforniaUnited States
University of California, DavisSacramentoCaliforniaUnited States
Washington University in St. LouisSt LouisMissouriUnited States
Nationwide Children's HospitalColumbusOhioUnited States
Neurology Rare Disease CenterFlower MoundTexasUnited States
Children's Hospital of The King's DaughtersNorfolkVirginiaUnited States

Official Trial Information

View on ClinicalTrials.gov

Data sourced from ClinicalTrials.gov. Last updated: April 14, 2026