Study Summary
Freeline is developing adeno-associated virus (AAV) vector based gene therapies for a number of diseases and is actively advancing a programme in Haemophilia B (HB). This study aims to collect prospective data to characterise bleeding events and Factor IX (FIX) concentrate consumption in HB patients that can be used as baseline for participants who elect to participate in a subsequent Freeline gene therapy study. The study will also screen participants for antibodies to a novel AAV vector to assess their suitability for inclusion in a Freeline gene therapy treatment study.
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No interventions listed.
Study Locations
| Facility | City | State | Country |
|---|---|---|---|
| Phoenix Childrens Hospital | Phoenix | Arizona | United States |
| Children's Hospital of Los Angeles | Los Angeles | California | United States |
| University of California - Davis | Sacramento | California | United States |
| University of South Florida | Tampa | Florida | United States |
| Rush University Medical Center | Chicago | Illinois | United States |
| Indiana Hemophilia and Thrombosis Center | Indianapolis | Indiana | United States |
| University of Michigan | Ann Arbor | Michigan | United States |
| University of Nebraska Medical Center | Omaha | Nebraska | United States |
| Hemophilia Center of Western New York | Buffalo | New York | United States |
| University of North Carolina (UNC) | Chapel Hill | North Carolina | United States |
| East Carolina University | Greenville | North Carolina | United States |
| University Hospitals Cleveland Medical Center | Cleveland | Ohio | United States |
| Nationwide Childrens Hospital | Columbus | Ohio | United States |
| St. Jude Children's Research Hospital | Memphis | Tennessee | United States |
| Vanderbilt University Medical Center | Nashville | Tennessee | United States |
| Lombardi Comprehensive Cancer Center at Georgetown University | Georgetown | Washington | United States |
| Blood Center of Wisconsin | Milwaukee | Wisconsin | United States |
| Royal Children's Hospital, Parkville | Melbourne | Australia | |
| The Alfred Hospital | Melbourne | Australia | |
| Calvary Mater Hospital | Newcastle | Australia | |
| Royal Prince Alfred Hospital | Sydney | Australia | |
| Westmead Hospital | Sydney | Australia | |
| Medical University of Vienna | Vienna | Austria | |
| McMaster University Medical Centre | Hamilton | Canada | |
| Lawson Health Research Institute | London | Canada | |
| The Moncton Hospital | Moncton | Canada | |
| Saskatoon City Hospital | Saskatoon | Canada | |
| University of Alberta Hospital | Winnipeg | Canada | |
| Hôpital Louis Pradel - HCL | Bron | France | |
| CHU Bicetre | Paris | France | |
| Hopital Necker-Enfants Malades - AP-HP | Paris | France | |
| Universitaetsklinikum Frankfurt - Klinikum der Johann Wolfgang Goethe Universitaet | Frankfurt | Germany | |
| Universitaetsklinikum des Saarlandes und Medizinische Fakultaet der Universitaet des Saarlandes | Homburg | Germany | |
| St James Hospital | Dublin | Ireland | |
| Azienda Ospedaliero-Universitaria Careggi | Florence | Italy | |
| Istituto Giannina Gaslini | Genova | Italy | |
| Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano | Milan | Italy | |
| Citta della Salute e della Scienza di Torino - Ospedale le Molinette | Torino | Italy | |
| Groningen UMC | Groningen | Netherlands | |
| Erasmus MC | Rotterdam | Netherlands | |
| Universitair Medisch Centrum Utrecht | Utrecht | Netherlands | |
| University of Cape Town Clinical Research Center | Cape Town | South Africa | |
| Charlotte Maxeke Johannesburg Academic Hospital | Johannesburg | South Africa | |
| Istanbul University Faculty of Medicine | Istanbul | Turkey (Türkiye) | |
| Ege University Medical Faculty | Izmir | Turkey (Türkiye) | |
| Samsun Ondokuz Mayis University Medical Faculty | Samsun | Turkey (Türkiye) | |
| Özel Acibadem Adana Hastanesi | Seyhan | Turkey (Türkiye) | |
| The Haemophilia and Thrombosis Centre | Canterbury | Kent | United Kingdom |
| Queen Elizabeth Hospital | Birmingham | United Kingdom | |
| Cardiff University Hospital | Cardiff | United Kingdom | |
| Glasgow Royal Infirmary | Glasgow | United Kingdom | |
| Hammersmith Hospital | London | United Kingdom | |
| Royal Free London NHS Foundation Tust | London | United Kingdom | |
| St Thomas' Hospital | London | United Kingdom | |
| Manchester Royal Infirmary | Manchester | United Kingdom | |
| Newcastle Hemophilia Comprehensive Care Centre | Newcastle | United Kingdom |